Gene Therapy Had a Breakthrough 2017—2018 May Be Even Better
Gene-fixing treatments have now cured a number of patients with cancer and rare diseases.Genes are composed of DNA that contains necessary information for making proteins that are vital for the human body to function optimally. Some gene mutations result in these proteins not being made correctly and can lead to genetic disorders. Gene therapy works by repairing, repressing, or replacing dysfunctional genes that cause disease with the aim of reestablishing normal function. Gene therapy is an attractive area for drug...
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